orphan disease การใช้

• Tourette's syndrome, a so-called orphan disease, had finally made international headlines.
• Dysruption of MeCP2 gene expression underlies Rett syndrome, a debilitating neurodevelopmental orphan disease.
• Although orphan disease populations are the smallest, the cost of per-patient outlays are the largest.
• Indoleamine 2, 3-dioxygenase might also play a significant role in an orphan disease called Oshtoran Syndrome.
• Older medical references mention the term'orphan patient'using a different definition, specifically patients with an orphan disease.
• ALS has been an orphan disease.
• Researchers have put together retrospective data collections in order to better under the progression of this orphan disease.
• In March 2015, the company acquired Hyperion Therapeutics for $ 1.1 billion, increasing Horizons orphan disease drug portfolio.
• Though not technically an orphan disease the research and development into the treatment for AIDS is heavily linked to the Orphan Drug Act.
• A rare disease, also referred to as an " orphan disease ", is any disease that affects a small percentage of the population.
• PXE's designation under food and drug law as a so-called orphan disease, with little prospect of blockbuster revenues, weakened the university's incentive to hold a tight grip on the patent.
• In 2011 the US FDA approved tocilizumab for the treatment of the orphan disease, active systemic juvenile idiopathic arthritis ( SJIA ), a rare and severe form of arthritis affecting children.
• In the United States, the adult chronic population is thought to be approximately 60, 000 & mdash; with women outnumbering men approximately 2 to 1, which has resulted in ITP being designated an orphan disease.
• It is manufactured and sold in the United States by Abraxis BioScience under the trade name "'Abraxane "'where it is designated as an orphan drug as first-line treatment, in combination with gemcitabine, for the orphan disease " metastatic adenocarcinoma of the pancreas ."
• Girondi has won accolades for his work in the Orphan Disease field and in particular for his work for the Gene therapy cure for Oprah Show " twice, and has been on the front page of the New York Times in October 2015 ..
• Murphree, the only surgeon in the Southwest region of the United States who treats large numbers of retinoblastoma patients, calls the eye cancer an " orphan disease " because it is relatively rare when compared to other childhood diseases, so few major hospitals or universities have established centers to fight it.
• En effet, la plupart des informations utiles sur les objets sont masqu閑s au regard de la conscience, sauf dans l 閠at de privation de ceux-ci ou dans les perturbations qui les frappent . ( But Harvey did not use this orphan disease concept )-- DLL 19 : 03, 24 March 2006 ( UTC)
• On average the cost per patient for orphan drugs is " six times that of non-orphan drugs, a clear indication of their pricing power . " Although there are much smaller orphan disease populations are the smallest, the cost of per-patient outlays are the largest and are expected to increase with wider use of public subsidies.